Bone development Bioinformatics Diseases Cell reprogramming MRI ERK1/2 signaling Genetical therapy CNS Neuromuscular disease DPRs ASO Skeletal muscle Gene transfer Disease heterogeneity GeneRide Chondrocytes Long-term handicap Brain MRI 3xTgAD Mice Clinical trials Cofilin-1 Maternal malnutrition G-Secretase Glucocorticosteroid AICD Cellules souches musculaires Albumin gene targeting Bone involvement FTD IUGR C9orf72 Fabry disease lysosomal storage disorders adeno asociated virus-9 Mouse model Early-onset sepsis Adult patients Dicer Calcium handling GABA Adult SMA IRM SMN Brain imaging Dilated cardiomyopathy Cartilage and bone regeneration Extremely preterm infants MND Functional outcomes Modèle murin FGR Antisense oligonucleotides Blood brain barrier CRISPR/SaCas9 Distal myopathy Les paramètres respiratoires Biological marker Lentiviral vectors Intra-CSF delivery Disease modifiers Gene therapy Duchenne Muscular Dystrophy MiRNA Amyotrophic Lateral Sclerosis Melatonin Errance diagnotique Prematurity IPSCs Clinical markers DTI AAV Mecp2 Amyotrophie spinale Brain damage Inflammation Longitudinal progression MUNIX Icv Brain injury MRNP assembly Clinical trial Biomarkers Effector T cells Adenosine ASOs FOXO3a Brain Brain development Epigenetic changes Biomarker Spinal muscular atrophy Microglia Genetics Maternal behavior Coagulation factor IX ALS Aav10 Fetal growth restriction Maladie neuromusculaire Intra-uterine growth restriction LMNA Cell stemness