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Publications du laboratoire Translational Research in Gene Therapy (UMR_S 1089-TARGET)

 

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AAP Baculovirus expression vector Intra-cerebrospinal fluid injection Duchenne Childhood blindness Genes In vivo AAV vectors Treg Duchenne muscular dystrophy Clinical trial Immunosuppression B-Lymphocytes/immunology/metabolism Homogeneity Bioconjugates Capsid thermostability Innate immunity Acute treatment Assembly-activating protein Homopolymers Inherited retinal dystrophies Exon skipping GRMD dog Adenoassociated viral vector Age Centronuclear myopathy Immunogenicity inflammation gene therapy AAV Mice High-throughput technology AAV Antibodies/immunology/metabolism Cone photoreceptors Manufacturing Intrathymic gene transfer GRMD Tolerance Insect cells Gene-therapy High-throughput sequencing CD8 + T lymphocytes Immune response Immunogenicity Inflammation Calcium Ectopic expression Cell–virus interaction Exercise Analytical ultracentrifugation Animal model DMD CNS Gene therapy Air tamponade Identity Immune responses Quality control Vector Antibody responses Adenoviridae/immunology ABCA4 Clinical trials Homologous recombination AUC GC-content Gene transfer Intravitreal Animals Adeno-associated virus Fluid-air exchange Infectivity Congenital amaurosis Cerebellum Eye surgery Human-monocyte-derived dendritic cells DMDmdx rat Beta-subunit Dynamin 2 Gene Transfer Discriminant analysis Gene Therapy Crigler–Najjar Syndrome Engineering Baculovirus Impurities Capsid Gait assessment Click chemistry Bioorthogonality Dose study Capsid assembly Skeletal muscle Humoral immunity Capsid thermal stability AAV vector Cell therapy Accelerometry Immunomodulation Identity assay CMC Dystrophin